2020
Dean R, Arjunji R, Awano H, Igarash A, Tanaka A, Jensen IS , Cyr PL et al. Cost-effectiveness of onasemnogene abeparvocec (ZOLGENSMA) for spinal muscular atrophy type 1 against nusinersen in Japan. ISPOR 25th Annual International Meeting, Orlando FL, 2020.
Publication: Abstracts and Presentations
/ Topics: Epidemiology , Health Economics and Outcomes Research (HEOR)
Miller B, Jensen IS , Dean R, Cyr PL , Slocomb T, James E, Beggs AH. Health resource use in patients with x-linked myotubular myopathy (XLMTM): Data from the RECENSUS Study. ISPOR 25th Annual International Meeting, Orlando FL, 2020.
Publication: Abstracts and Presentations
/ Topics: Epidemiology
Sacks NC , Healey B, Cyr PL , Graham R. Economic burden of X-linked myotubular myopathy (XLMTM) by ventilation status. ISPOR 25th Annual International Meeting, Orlando FL, 2020.
Publication: Abstracts and Presentations
/ Topics: Epidemiology
Miller B, Yao W, Dean R, Jensen I , Cyr PL , Slocomb T. Understanding the impact of XLMTM on parents and caregivers in the US: An analysis of survey results. ISPOR 18th Annual European Meeting, Milan Italy, 2020.